Tazobactam

證據等級: L5 預測適應症: 10

目錄

  1. Tazobactam
  2. Tazobactam: From Beta-Lactamase Inhibitor (Combination Therapy) to Pneumonia
    1. One-Sentence Summary
    2. Quick Overview
    3. Why is This Prediction Reasonable?
    4. Clinical Trial Evidence
    5. Literature Evidence
    6. South Africa Market Information
    7. Safety Considerations
    8. Conclusion and Next Steps
    9. Disclaimer

## 藥師評估報告

Tazobactam: From Beta-Lactamase Inhibitor (Combination Therapy) to Pneumonia

One-Sentence Summary

Tazobactam is a beta-lactamase inhibitor with no antibacterial activity on its own; it is always used in fixed combinations (e.g. Piperacillin-Tazobactam, Ceftolozane-Tazobactam) to restore the killing power of a partner beta-lactam against beta-lactamase-producing (including ESBL) bacteria. The TxGNN model predicts continued/expanded relevance for Pneumonia (including hospital-acquired and ventilator-associated pneumonia), with 57 clinical trials and 20 publications currently identified in this evidence pack supporting this direction.

Quick Overview

Item Content
Original Indication No standalone indication — Tazobactam is used only as the beta-lactamase-inhibitor component of combination antibiotics (e.g. Piperacillin-Tazobactam, Ceftolozane-Tazobactam)
Predicted New Indication Pneumonia (incl. hospital-acquired / ventilator-associated pneumonia)
TxGNN Prediction Score 99.46%
Evidence Level L1
South Africa Market Status Not Marketed
Number of SAHPRA Registrations 0
Recommended Decision Proceed with Guardrails

Why is This Prediction Reasonable?

Currently, detailed mechanism of action data for Tazobactam itself is not available. Based on known pharmacology, Tazobactam is a beta-lactamase inhibitor that has no clinically meaningful antibacterial activity alone. It is always co-administered with a beta-lactam partner drug — most commonly piperacillin or ceftolozane — to inhibit bacterial beta-lactamase enzymes (including extended-spectrum beta-lactamases, ESBLs), thereby restoring the partner drug’s bactericidal activity against beta-lactamase-producing strains.

Pneumonia, particularly hospital-acquired and ventilator-associated pneumonia, is frequently caused by Gram-negative pathogens such as Klebsiella pneumoniae, Escherichia coli, and Pseudomonas aeruginosa — organisms commonly implicated in beta-lactamase-mediated resistance. This mechanistic profile aligns directly with the pathogen spectrum seen in nosocomial pneumonia.

Critically, this is not a novel repurposing hypothesis in the strict sense: Piperacillin-Tazobactam and Ceftolozane-Tazobactam are already established, guideline-referenced therapies for hospital-acquired and ventilator-associated bacterial pneumonia, and are used repeatedly as the active comparator arm in pivotal Phase 3 trials of newer beta-lactam/beta-lactamase-inhibitor combinations (e.g. imipenem/cilastatin/relebactam, ceftolozane/tazobactam vs. meropenem). This confirms the mechanistic and clinical plausibility of the TxGNN prediction.

Clinical Trial Evidence

Trial Number Phase Status Enrollment Key Findings
NCT03583333 Phase 3 Completed 274 Multinational double-blind RCT: imipenem/cilastatin/relebactam vs. piperacillin/tazobactam in HABP/VABP; non-inferiority on 28-day all-cause mortality
NCT02493764 Phase 3 Completed 537 Double-blind active-comparator RCT: imipenem/cilastatin/relebactam vs. piperacillin/tazobactam in HABP/VABP
NCT02070757 Phase 3 Completed 726 Double-blind RCT: ceftolozane/tazobactam vs. meropenem in ventilated nosocomial pneumonia; non-inferiority on Day 28 all-cause mortality
NCT00253955 Phase 3 Completed 460 Open-label RCT: levofloxacin vs. piperacillin/tazobactam in mild-to-moderate hospital-acquired pneumonia
NCT01796717 Phase 2/3 Unknown 50 Prolonged vs. intermittent infusion of piperacillin/tazobactam for nosocomial pneumonia in ICU; clinical, bacteriologic and PK/safety endpoints
NCT01853982 Phase 3 Terminated 4 Randomized open-label study: IV ceftolozane/tazobactam vs. IV piperacillin/tazobactam in ventilator-associated pneumonia (terminated early, low enrollment)
NCT03897582 N/A Recruiting 65 Beta-lactam (incl. piperacillin/tazobactam) dosing in ICU pneumonia patients on continuous renal replacement therapy
NCT03581370 Phase 3 Recruiting 80 Short vs. prolonged infusion of ceftolozane-tazobactam in VAP due to Pseudomonas aeruginosa
NCT04223752 Phase 1 Completed 41 Safety, tolerability and PK of ceftolozane/tazobactam in pediatric nosocomial pneumonia
NCT04986254 N/A Completed 179 Individualised dosing regimens (incl. piperacillin/tazobactam) to maximise antibiotic effectiveness in ICU pneumonia

Literature Evidence

PMID Year Type Journal Key Findings
30208454 2018 RCT JAMA Piperacillin-tazobactam vs. meropenem for 30-day mortality in ceftriaxone-resistant E. coli/K. pneumoniae bloodstream infection
31563344 2019 RCT Lancet Infect Dis ASPECT-NP: ceftolozane-tazobactam vs. meropenem for nosocomial pneumonia, Phase 3 non-inferiority trial
39674398 2025 RCT Int J Infect Dis Phase 3 non-inferiority trial: imipenem/cilastatin/relebactam vs. piperacillin/tazobactam in HABP/VABP
32785589 2021 RCT Clin Infect Dis RESTORE-IMI 2: randomized double-blind multicenter trial of imipenem/cilastatin/relebactam vs. piperacillin/tazobactam in HABP/VABP
32662691 2020 Review Expert Rev Anti Infect Ther Review of ceftolozane/tazobactam for treatment of hospital-acquired pneumonia
38823453 2024 Review Clin Microbiol Infect Systematic review and network meta-analysis of empiric antibiotic regimens in non-ventilator-associated HAP
35488823 2022 Review Rev Esp Quimioter Review of ceftolozane-tazobactam in nosocomial pneumonia
38971203 2024 Review Int J Antimicrob Agents Systematic review of PK/PD of novel beta-lactams and beta-lactam/beta-lactamase-inhibitor combinations in pneumonia from carbapenem-resistant Gram-negative bacteria
39701120 2025 Observational Lancet Infect Dis CACTUS: multicentre retrospective comparison of ceftazidime-avibactam vs. ceftolozane-tazobactam for MDR P. aeruginosa infections
34598422 2021 Review Rev Esp Quimioter When, how and why to use ceftolozane-tazobactam

South Africa Market Information

Tazobactam has no active SAHPRA registrations and is currently classified as Not Marketed in South Africa (0 registered products in this evidence pack). No product name, dosage form, or approved indication text is available to report.

Safety Considerations

Please refer to the SAHPRA-approved Professional Information (PI) for safety information. Report adverse drug reactions to SAHPRA.

Conclusion and Next Steps

Decision: Proceed with Guardrails

Rationale: Multiple completed Phase 3 RCTs (e.g. NCT03583333, NCT02493764, NCT02070757, NCT00253955) establish beta-lactam/beta-lactamase-inhibitor combinations containing tazobactam as a validated, guideline-referenced comparator for hospital-acquired and ventilator-associated pneumonia, giving strong (L1) mechanistic and clinical evidence. However, Tazobactam has no current SAHPRA registration in South Africa, and TFDA/SAHPRA-level safety data (warnings, contraindications) and detailed MOA data are both marked as data gaps — one of them (PI warnings/contraindications) is classified as Blocking for safety pre-assessment.

To proceed, the following is needed:

  • SAHPRA-approved Professional Information (PI) — warnings, precautions, and contraindications (Blocking data gap DG001)
  • Detailed mechanism of action data from DrugBank (High-priority data gap DG002)
  • Confirmation of regulatory pathway/status for tazobactam-containing combination products (e.g. Piperacillin-Tazobactam) intended for the South African market
  • A drug-drug interaction (DDI) profile, currently unavailable (“not_found”)

    Disclaimer

This content is for research purposes only and does not constitute medical advice. Clinical validation is required before any clinical application.



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